A Valentine's card exchanged reminded columnist Halsey Blocher that disabled people also deserve opportunities to serve ...

The U.S. Food and Drug Administration (FDA) has approved a new tablet formulation of Evrysdi (risdiplam), an approved oral ...

Columnist Helen Baldwin reflects on a quarter century of changes in the SMA community and honors the memory of two ...

Spinraza treatment does not lead to significant kidney dysfunction in SMA patients with types 1 and 2, a safety and efficacy ...

Metabolic abnormalities, including the buildup of fat in the liver and other issues, occur before the loss of motor neurons, according to a study in a mouse model of spinal muscular atrophy (SMA). The ...

For columnist Alyssa Silva, advances in the development of SMA treatments have felt like glimmers of miracles.

Cure SMA is leading an advocacy campaign seeking new research funding to address unmet challenges for people with SMA.

Study using a new, child-friendly scale found patients up to age 2 had smaller mouth openings than healthy peers, risking ...

In surveys, parents of children with SMA and healthcare professionals in Sweden note the many ways the pandemic affected ...