Columnist Michelle Harlan has set some health goals for the new year, and to her delight, they're not that different from ...
Self-advocacy skills help to build confidence and reduce feelings of helplessness, writes columnist. It's good to start young ...
Emmaus Life Sciences has entered into an agreement to sell the North American rights to its oral sickle cell disease ...
SCD gene therapy approaches using CRISPR, gene therapy, and base editing show different stem cell outcomes in a mouse study.
Whenever I’m asked to list the symptoms of sickle cell disease (SCD), I am always confused about where to begin. The condition is fundamentally a blood disorder, and every organ needs a steady supply ...
On Dec. 8, the U.S. Food and Drug Administration (FDA) approved two cell-based gene therapies for sickle cell disease (SCD), a groundbreaking decision that now offers patients more than one ...
A program that provides integrated primary and specialist care for adults with sickle cell disease (SCD) significantly reduced emergency department visits, according to a study from Massachusetts ...
The European Medicines Agency (EMA) has confirmed the continuing suspension of marketing authorization for Pfizer’s sickle cell disease (SCD) treatment Oxbryta (voxelotor) — withdrawn from the market ...
The first sickle cell disease (SCD) patient has been enrolled in a Phase 1b clinical trial evaluating iadademstat, Oryzon Genomics‘ investigational oral therapy designed to boost fetal hemoglobin (HbF ...
Disc Medicine says it’s planning to launch a clinical trial before the end of the year that will test DISC-3405, its treatment candidate for reducing high iron levels and easing iron overload, in ...
Every year on my Twitter feed, I see a tweet about how important it is to know your genotype, as well as your partner’s. I agree with the rationale for this; it’s important to be as prepared as you ...